Transforming Lives
Innovation, fueled by science and a passion for patients
PTC is an established global biopharmaceutical company that delivers transformative therapies for people living with rare diseases. For 25 years, we have been harnessing our scientific platforms to create new therapies that address the underlying cause of the disease and deliver on our promise to create more moments for those who count on us.
Focused research platforms at work for patients
Challenging what's possible
Harnessing groundbreaking science for patients has led to many firsts – the first approved treatment for Duchenne in the world, the first approved gene therapy directly infused into the brain, and the first approved small molecule splicing modifier. Our innovative pipeline continues to expand as we discover and develop treatments using the newest technologies available.
Clinical Trials
Click the links below to learn more about our actively enrolling trials
We love what we do
PTC employees are working to change patients’ lives every single day.
We are motivated by our patients and the drive for them to have more moments with their families, made possible in part by our research and therapies.
If you’re looking to take on rewarding work with inspiring colleagues, come grow with us.
Making headlines
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PRESS RELEASE
PTC Therapeutics Announces European Commission Returns Translarna™ Opinion to CHMP For Re-evaluation
PTC Therapeutics announced today that the European Commission (EC) has decided not to adopt the CHMP's negative opinion of January 24, 2024 on the annual renewal of the conditional marketing authorization of Translarna™ (ataluren) and has returned the opinion to the CHMP for re-evaluation. -
NEWSROOM
Highlighting Voices of the HD Community
In honor of Huntington’s disease (HD) Awareness Month, we are highlighting inspiring and impactful voices from the HD community. Watch our video to learn more about this rare, hereditary, genetic disorder of the central nervous system, and hear from the global community about their hope for the future of HD. -
NEWSROOM
PTC Wins Gallup’s 2024 Don Clifton Strengths-Based Culture Award
PTC has been named a winner of the 2024 Don Clifton Strengths-Based Culture Award from Gallup for the third time. This award recognizes organizations with strong workplace cultures that get the best out of their employees by developing their strengths and placing them at the center of how they work every day.