Translarna™ (ataluren)* has been approved in the European Union for ambulatory patients aged 5 years and older with Duchenne muscular dystrophy resulting from a nonsense mutation in the dystrophin gene.

Translarna Summary of Product Characteristics

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*Translarna is an investigational new drug in the US



EMFLAZA® (deflazacort) is approved in the US for the treatment of Duchenne muscular dystrophy in patients 5 years of age and older.

Please see the accompanying full Prescribing Information

Click here for Important Safety Information

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For medical information, product complaints, or to report an adverse event, please call 1‑866‑562‑4620.

You may report adverse events to FDA at 1‑800‑FDA‑1088 or


TEGSEDI™ (inotersen): has received marketing authorisation approval from the European Commission (EC) for the treatment of stage 1 or stage 2 polyneuropathy in adult patients with hereditary transthyretin amyloidosis (hATTR). PTC will commercialize TEGSEDI™ (inotersen) in Latin America (LATAM).

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