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NDA Submission for the Treatment of Children and Adults living with Friedreich Ataxia

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The latest news from PTC

  1. Rare Journeys - Marharyta

    Raising Awareness of Duchenne in Ukraine

    Marharyta has worked tirelessly to improve her son’s life and raise awareness of Duchenne.
    Rare Disease Community, Rare Journeys
    January 16, 2021
    1 minute
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  2. Rare Journeys - Bjorn

    Breaking Down Physical and Digital Barriers

    Björn doesn’t let his Duchenne diagnosis stop him from empowering others like him.
    Rare Disease Community, Rare Journeys
    January 12, 2021
    2 minutes
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