The latest news from PTC

Clinical trials provide the medical community with valuable research and data that helps to facilitate the development of new and potentially life-saving therapies. By participating in a clinical trial, you are taking an active role in the development and approval of new medicines and treatments. There is a lot to learn about clinical trials –…

An Informative Q&A with Jonathan Cherry, Global Project Leader Our research efforts at PTC are focused on two scientific platforms – splicing and ferroptosis and inflammation – where PTC has unique expertise to discover and advance innovative therapies to the clinic. We recently sat down with Jonathan Cherry, Global Project Leader, to learn more about…

In honor of Huntington’s disease (HD) Awareness Month, we are highlighting inspiring and impactful voices from the HD community. Watch the video below to learn more about this rare, hereditary, genetic disorder of the central nervous system, and hear from the global community about their hope for the future of HD.

We are excited to announce that PTC has been named a winner of the 2024 Don Clifton Strengths-Based Culture Award from Gallup. This is the third time PTC has won this award that recognizes organizations with strong workplace cultures that get the best out of their employees by developing their strengths and placing them at…

At PTC, we strive to be good citizens of the world and make change for a better planet, because as a science-based company, we understand the impact people have on the environment. We pride ourselves not only on our innovative work but on our commitment to sustainability and social responsibility. To bring this mission to…

Our research efforts at PTC are focused on two scientific platforms – splicing and ferroptosis and inflammation – where PTC has unique expertise to discover and advance innovative therapies to the clinic. We recently sat down with Jeff Trimmer, Senior VP, Research Site Head, to learn more about ferroptosis, how it relates to inflammation and…

When asked why it’s important to recognize Women’s History Month (WHM) in March, women leaders at PTC agree: WHM is a significant moment in time to honor the achievements and impact of women across history. “Women’s History Month demonstrates the vast contributions women have made across all areas – politics, music, fine arts, drama, literature,…

Rare Disease Day, which takes place every year on the last day of February, is a global movement aimed at raising awareness of the 7,000+ rare diseases and more than 300 million people worldwide who live with a rare disease. With our deep experience in the rare disease space for more than 25 years and…

In this podcast episode we are discussing the topic of Nutrition and Duchenne with our guest speaker, Dr. Kindann Fawcett, Behavioral Health Scientist, Dietitian and Caregiver to her son with Duchenne Muscular Dystrophy.  Our conversation with Dr. Kindann Fawcett explores; Tune in to learn more about this topic. Visit the Take on Duchenne: North America…

There are many things that make PTC Therapeutics truly unique, and the splicing platform is one of them. Here, “splicing” refers to PTC’s scientific platform that takes aim at modulating pre-messenger RNA (pre-mRNA) splicing to control protein production. This scientific platform together with the technology that powers it, enables the identification of small molecules, which…