Transforming Lives
Innovation, fueled by science and a passion for patients
PTC is an established global biopharmaceutical company that delivers transformative therapies for people living with rare diseases. For 25 years, we have been harnessing our scientific platforms to create new therapies that address the underlying cause of the disease and deliver on our promise to create more moments for those who count on us.
Focused research platforms at work for patients
Challenging what's possible
Harnessing groundbreaking science for patients has led to many firsts – the first approved treatment for Duchenne in the world, the first approved gene therapy directly infused into the brain, and the first approved small molecule splicing modifier. Our innovative pipeline continues to expand as we discover and develop treatments using the newest technologies available.
Clinical Trials
We are committed to making progress in rare disease through clinical trial research.
We love what we do
PTC employees are working to change patients’ lives every single day.
We are motivated by our patients and the drive for them to have more moments with their families, made possible in part by our research and therapies.
If you’re looking to take on rewarding work with inspiring colleagues, come grow with us.
![PTC Lab Employees](https://www.ptcbio.com/wp-content/uploads/sites/2/2024/07/Lab_Employees2024-1024x512.png)
Making headlines
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PRESS RELEASE
PTC Therapeutics to Participate at Upcoming Investor Conferences
PTC Therapeutics announced that the company will present a company overview at three upcoming investor conferences on Sept. 5, Sept. 6, and Sept. 17. The presentations will be webcast live on the Events and Presentations page under the Investor section of PTC Therapeutics' website and will be archived for 30 days following the presentation. -
NEWSROOM
Raising Voices for Duchenne
World Duchenne Awareness Day is on Sept. 7. In honor of this year’s theme, “raise your voice for Duchenne”, we are highlighting remarkable individuals in the Duchenne community who are doing just that: using their voices to raise awareness of Duchenne, advocating for those living with the condition and inspiring the community to join them in amplifying their voices. -
NEWSROOM
Checking In with Emerging Leaders at PTC
The Emerging Leaders program was created specifically for individuals at PTC who demonstrate the passion and traits to become successful future leaders. Earlier this year, the company celebrated its third cohort of Emerging Leaders. We checked in with graduates from all three cohorts to learn more about their ELP experience, their biggest takeaways, and how the program prepared them for future leadership roles.